Science & Nature · 2
What did Casgevy become in 2023-2024, marking a historic medical milestone?
Answer
First CRISPR-based gene therapy approved for human use
Casgevy became the first-ever CRISPR-based therapy approved for human use, gaining UK approval in November 2023 and FDA approval in December 2023 for treating sickle cell disease. During 2024, it received approval across the UK, US, EU, Bahrain, Saudi Arabia, and Canada. This landmark achievement represents the culmination of decades of gene-editing research and opens doors to treating genetic diseases at their source.
💡 Did you know?
Casgevy uses CRISPR-Cas9 to edit patients' own blood cells, eliminating the genetic cause of sickle cell disease rather than just treating symptoms.
Other options people guess
- First AI-designed antibiotic
- First personalized cancer vaccine
- First synthetic organ transplant
Topics
- genetics
- CRISPR
- gene-therapy
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